PTC Therapeutics' Kebilidi gains FDA accelerated approval as the first brain-administered gene therapy in the U.S. for AADC ...

FDA supports CaaMTech's CT-4201 psilocin program for depression, advancing psychedelic therapy and clearing key regulatory ...

The FDA designated 166 products under its breakthrough devices program in its most recent financial year, reversing the ...

In a new study, researchers at McMaster University have identified a potential treatment for Sandhoff and Tay-Sachs ...

The FDA has followed in the footsteps of its European counterparts and granted accelerated approval to PTC Therapeutics’ gene ...

The boundary between science fiction and medical reality blurs as companies like Elon Musk's Neuralink make strides in ...

Investors are responding to Tesla CEO Elon Musk's close association with President-elect Donald Trump, anticipating a ...

QIAGEN's QIAstat-Dx Meningitis/Encephalitis Panel has received FDA clearance, enabling faster and more accurate diagnosis of ...

Shortly after 2 a.m. on a Saturday in a midtown Manhattan sports bar packed with Aussies, Dr. Tom Oxley was feeling stunned.

Research studies explore the different factors that affect health and lead to disease. Clinical trials test the safety and effectiveness of new cancer drugs and treatments. They help us find better ...

Pfizer Inc. has won regulatory approval for its hympavzi drug as a treatment for hemophilia A or B without inhibitors — making it the first antitissue-factor pathway inhibitor to be allowed for ...

Science Corporation's retinal implant allowed some people who lost their central vision to read, play cards, and recognize faces.